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Glafabra Therapeutics Receives FDA Orphan Drug Designation for GT-GLA-S03, Advancing a Redosable Cell Therapy for Fabry Disease

For Fabry patients, a potential path to converting 130 clinic visits into one treatment every five years.

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Glafabra Therapeutics, Uncommon Cures Collaborate to Advance Fabry Disease Therapy

Glafabra Therapeutics, Uncommon Cures Collaborate to Advance Fabry Disease Therapy

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